Genetic Disorder

Quoin Outlicenses Lead Asset For Skin Disorder In Middle East, North Africa

Quoin, AFT Pharmaceuticals Ink Licensing Pact For Lead Candidate In Genetic Skin Disease

Jennifer Doudna Spinout Mammoth Inks $700M CRISPR Deal With Vertex

Quoin, AFT Pharmaceuticals Ink Licensing Pact For Lead Candidate In Genetic Skin Disease

Jennifer Doudna Spinout Mammoth Inks $700M CRISPR Deal With Vertex

Stealth Bio Stock Falls On FDA Refusal to File Letter For Barth Syndrome Candidate

PTC Therapeutics' Rare Genetic Disease Gene Therapy Shows Durable Improvement Even At 5 Years

Stealth Bio Stock Falls On FDA Refusal to File Letter For Barth Syndrome Candidate

PTC Therapeutics' Rare Genetic Disease Gene Therapy Shows Durable Improvement Even At 5 Years

Eli Lilly Inks Another RNA Collab, This Time With ProQR

AstraZeneca's Drug Shows Promise In Copper Build-Up Genetic Disease

Genetic Disorder Recent News

Stealth Bio Files US Application For Ultra Rare Genetic Disease Candidate

PTC Therapeutics' Waylivra Scores Approval In Brazil For Genetic Disorder

Cyclo Therapeutics' Trappsol Shows Early Safety, Efficacy In Genetic Disorder

AstraZeneca's Koselugo Gets European Nod To Treat Children With Multisystem Genetic Disorder